Antisense-oligonucleotide therapeutic - AcuraStem
Alternative Names: Frontotemporal dementia ASO - AcuraStemLatest Information Update: 31 Mar 2023
At a glance
- Originator AcuraStem
- Class Antidementias; Antisense oligonucleotides
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Frontotemporal dementia
Most Recent Events
- 30 Mar 2023 Preclinical trials in Frontotemporal dementia in USA (Parenteral) (AcuraStem pipeline, March 2023)