AX 1412
Alternative Names: AX-1412Latest Information Update: 14 Apr 2023
At a glance
- Originator ProQR Therapeutics
- Class Cardiovascular therapies; RNA
- Mechanism of Action Beta-1,4-galactosyltransferase I expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Cardiovascular disorders