AX 2911
Alternative Names: AX-2911Latest Information Update: 21 May 2026
At a glance
- Originator ProQR Therapeutics
- Class Hepatoprotectants; Oligonucleotides
- Mechanism of Action Adiponutrin expression modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Non-alcoholic steatohepatitis
Most Recent Events
- 12 May 2026 ProQR Therapeutics plans to initiate a first-in-human (FIH) IIT trial in the first half of 2027
- 11 May 2026 Pharmacodynamics data from a preclinical studies in Nonalcoholic steatohepatitis released by ProQR Therapeutics
- 12 Mar 2026 Pharmacodynamics data from a preclinical studies in Nonalcoholic steatohepatitis released by ProQR Therapeutics