AX 9115
Alternative Names: AX-9115Latest Information Update: 25 Apr 2023
At a glance
- Originator ProQR Therapeutics
- Class Oligonucleotides
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Metabolic disorders
Most Recent Events
- 18 Apr 2023 ProQR Therapeutics has patent protection for Axiomer® platform in China, Canada, Israel, New Zealand, Japan, Russia, South Africa, the US and Europe
- 05 Apr 2023 Early research in Metabolic disorders in Netherlands (Parenteral)
- 31 Dec 2022 ProQR Therapeutics has patent pending for Axiomer® platform in Australia, Brazil, India, and the US (divisional application)