Neurodegenerative disorder therapeutic - Alexion AstraZeneca Rare Disease
Latest Information Update: 26 Apr 2023
At a glance
- Originator Alexion AstraZeneca Rare Disease
- Class Proteins
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Neurodegenerative disorders
Most Recent Events
- 03 Apr 2023 JCR Pharmaceuticals and Alexion AstraZeneca Rare Disease enters into a research collaboration, option and license agreement to develop an protein therapeutic molecule for Neurodegenerative disease
- 03 Apr 2023 Early research in Neurodegenerative disorders in USA (unspecified route)
- 29 Jun 2015 JCR Pharmaceuticals has patent pending for J-Brain Cargo®, blood-brain barrier (BBB) penetration technology