AXV 102
Alternative Names: AXV-102Latest Information Update: 02 May 2024
At a glance
- Originator Axovia Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Bardet-Biedl Syndrome
Most Recent Events
- 06 Apr 2023 Axovia Therapeutics plans a First in Human trial for Bardet-Biedl syndrome in mid 2025 (Axovia Therapeutics pipeline, April 2024)
- 06 Apr 2023 Preclinical trials in Bardet-Biedl Syndrome in United Kingdom (Parenteral) before April 2023 (Axovia Therapeutics pipeline, April 2023)
- 06 Apr 2023 Pharmacodynamics data from preclinical studies in released by Axovia Therapeutics before April 2023 (Axovia pipeline, April 2023)