OCU 410 ST
Alternative Names: AAV5-hRORA; OCU-410-STLatest Information Update: 03 Apr 2024
At a glance
- Originator Schepens Eye Research Institute
- Developer Ocugen
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference; Nuclear receptor subfamily 1 group F member 1 replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Stargardt disease
- Preclinical Cone rod dystrophies; Retinitis pigmentosa
Most Recent Events
- 01 Apr 2024 Adverse event data from the phase I/II GARDian trial in Stargardt disease released by Ocugen
- 25 Aug 2023 Phase-I/II clinical trials in Stargardt disease (In children, In adults) in USA (Subretinal) (NCT05956626)
- 21 Aug 2023 Ocugen plans phase-I/II trial for Stargardt disease by the end of 2023