Reasearch programme: renal disorders therapeutics - Exonate
Alternative Names: mRNA targeted therapies; mRNA targeted therapies ExonateLatest Information Update: 30 Jun 2023
At a glance
- Originator Exonate
 - Class Small molecules
 - Mechanism of Action Cyclin-dependent kinase-activating kinase modulators; RNA splicing modulators
 
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              Orphan Drug Status
              No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
 - New Molecular Entity Yes
 
Highest Development Phases
- Research Diabetic nephropathies
 
Most Recent Events
- 21 Apr 2023 Early research in Diabetic nephropathies in United Kingdom (unspecified route) (Exonate pipeline, April 2023)