GEN 6051
Alternative Names: Exon 51 skipping RNA; GEN-6051Latest Information Update: 28 May 2023
At a glance
- Originator Suzhou GenAssist Therapeutics
- Class Gene therapies
- Mechanism of Action Dystrophin expression modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 10 May 2023 Preclinical trials in Duchenne muscular dystrophy in China (Parenteral) (Suzhou GenAssist Therapeutics pipeline, May 2023)