Research programme: neurological and neuromuscular disease therapeutics - Prevail Therapeutics
Latest Information Update: 07 May 2025
At a glance
- Originator Prevail Therapeutics
- Class Gene therapies
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Neurological disorders
Most Recent Events
- 29 Apr 2025 Preclinical trials in Neurological disorders in USA (Parenteral), before April 2025
- 16 May 2023 Scribe Therapeutics enters into strategic collaboration with Prevail Therapeutics for Scribe’s CRISPR X-Editing (XE) technologies
- 16 May 2023 Early research in Neurological disorders in USA (Parenteral)