ADX 038
Alternative Names: ADX-038Latest Information Update: 06 Feb 2026
At a glance
- Originator ADARx Pharmaceuticals
- Class Oligonucleotides; Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase II Dry age-related macular degeneration; IgA nephropathy
- Phase I Paroxysmal nocturnal haemoglobinuria
Most Recent Events
- 10 Nov 2025 Phase-II clinical trials in Dry age-related macular degeneration in Australia (SC) (NCT06990269)
- 10 Nov 2025 Phase-II clinical trials in Dry age-related macular degeneration in Canada (SC) (NCT06990269)
- 10 Nov 2025 Phase-II clinical trials in Dry age-related macular degeneration in USA (SC) (NCT06990269)