ADX 038
Alternative Names: ADX-038Latest Information Update: 02 Jun 2025
At a glance
- Originator ADARx Pharmaceuticals
- Class Oligonucleotides; Small interfering RNA
- Mechanism of Action RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Paroxysmal nocturnal haemoglobinuria
Most Recent Events
- 25 May 2025 ADARx Pharmaceuticals plans phase-II trial for Membranous glomerulonephritis and IgA nephropathy in July 2025 (Unspecified) (NCT06989359),
- 25 May 2025 ADARx Pharmaceuticals plans a phase II trial for Dry age-related macular degeneration (SC) in August 2025 (NCT06990269)
- 03 Jul 2023 Phase-I clinical trials in Paroxysmal nocturnal haemoglobinuria (In adults) in Australia (unspecified route) (NCT05876312)