ASP 2957
Alternative Names: ASP-2957; KT-430; MyoAAV3.8-engineered-capsid-myosin-heavy-chain-kinase-7-human-myotubularin; MyoAAV3.8-MHCK7-hMTM1Latest Information Update: 04 Jun 2026
At a glance
- Originator Kate Therapeutics
- Developer Astellas Pharma; Kate Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference; Myotubularin replacements
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Congenital structural myopathies
Most Recent Events
- 15 Dec 2025 Phase-I/II clinical trials in Congenital structural myopathies (In neonates, In infants, In children) in USA, Canada (IV) (NCT07052929)
- 21 Nov 2024 Kate Therapeutics has been acquired by Novartis
- 08 Jun 2023 KT 430 licensed to Astellas Pharma worldwide for the treatment of Congenital structural myopathies of