BMN 333
Alternative Names: BMN-333; C-type natriuretic peptide; Long acting C-type natriuretic peptide (CNP); Long acting CNP - BioMarin PharmaceuticalsLatest Information Update: 11 Mar 2026
At a glance
- Originator BioMarin Pharmaceutical
- Class Natriuretic peptides
- Mechanism of Action Natriuretic peptide replacements
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Achondroplasia; Hypochondroplasia
Most Recent Events
- 02 Mar 2026 BioMarin Pharmaceutical plans phase-II/III ASPEN trial for Achondroplasia (Treatment-naive, In children, In Adolescents) (SC, Injection), (NCT07441876)
- 23 Feb 2026 BioMarin Pharmaceuticals plans a phase II/III trial for Achondroplasia in first half of 2026
- 31 Jan 2025 Phase-I clinical trials in Achondroplasia (unspecified route)