Research programme: AAV mediated cardiovascular gene therapies - BioMarin Pharmaceutical
Alternative Names: AAV CV gene therapy - BioMarin Pharmaceutical; AAV gene therapy; Adeno-associated virus (AAV) gene therapy; Adeno-associated virus (AAV) gene therapy- BioMarin Pharmaceutical; CV gene therapy - BioMarin PharmaceuticalLatest Information Update: 23 Apr 2024
At a glance
- Originator BioMarin Pharmaceutical
- Class Cardiovascular therapies; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Cardiovascular disorders
Most Recent Events
- 23 Apr 2024 Preclinical trials in Cardiovascular disorders in USA (Parenteral) (BioMarin Pharmaceutical pipeline, April 2024)
- 22 Jun 2023 Early research in Cardiovascular disorders in USA (Parenteral), prior to June 2023 (BioMarin Pharmaceutical pipeline, June 2023)