Duchenne muscular dystrophy gene therapy - Myogene
Alternative Names: MyoDys45-55 - MyogeneLatest Information Update: 17 Aug 2023
At a glance
- Originator Myogen
- Class Gene therapies
- Mechanism of Action Dystrophin expression stimulants; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Duchenne muscular dystrophy