Ataxia telangiectasia therapeutic - Insmed
Latest Information Update: 21 Sep 2023
At a glance
- Originator Insmed
- Class Gene therapies
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Ataxia telangiectasia
Most Recent Events
- 22 Aug 2023 Ataxia telangiectasia gene therapeutic - Insmed is available for licensing as of 22 Aug 2023. https://insmed.com/about/partnerships/
- 21 Aug 2023 Preclinical trials in Ataxia telangiectasia in USA (Parenteral) prior to August 2023 (Insmed pipeline, August 2023)