ASP 2016
Alternative Names: ASP-2016Latest Information Update: 22 Jan 2025
At a glance
- Originator Astellas Gene Therapies
- Class Gene therapies
- Mechanism of Action Frataxin protein replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Friedreich's ataxia
Most Recent Events
- 08 Jan 2025 Astellas Gene Therapies terminates a phase I trial in Friedreich's ataxia in USA (IV) due to the corporate decision not to initiate the trial at this time (NCT06483802)
- 08 Nov 2024 Astellas Gene initiates a Therapies phase-I clinical trials in Friedreich's ataxia in USA (IV) (NCT06483802)
- 03 Jul 2024 Astellas Gene Therapies plans a phase Ib trial for Friedreich's Ataxia in USA (IV, infusion) (NCT06483802)