ASP 2016
Alternative Names: ASP-2016Latest Information Update: 16 Jul 2024
At a glance
- Originator Astellas Gene Therapies
- Class Gene therapies
- Mechanism of Action Frataxin protein replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Friedreich's ataxia