Leber congenital amaurosis- gene therapy - IVERIC bio
Alternative Names: mini-CEP290; mini-CEP290 Iveric; mini-CEP290: LCA10Latest Information Update: 01 Dec 2023
At a glance
- Originator University of Massachusetts Medical School
- Developer IVERIC bio
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Cep290 protein modulators; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Leber congenital amaurosis
Most Recent Events
- 28 Aug 2023 Preclinical studies in Leber congenital amaurosis in USA (unspecified route) (Iveric Bio pipeline, August 2023)
- 11 Jul 2023 IVERIC bio has been acquired by Astellas Pharma
- 24 Mar 2023 IVERIC bio has patents pending for eye disorder gene therapies in USA, the EPO Countries, China, Japan and certain other jurisdictions, prior to December 2022