Stargardt disease - gene therapy - IVERIC bio
Alternative Names: mini-ABCA4; mini-ABCA4: STGD1; mini-ABCA4: STGD1 -IvericLatest Information Update: 16 Oct 2023
At a glance
- Originator University of Massachusetts Medical School
- Developer IVERIC bio
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action ABCA4 protein modulators; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Stargardt disease