CS 101
Alternative Names: CS-101Latest Information Update: 27 Aug 2024
At a glance
- Originator CorrectSequence Therapeutics
- Developer CorrectSequence Therapeutics; The First Affiliated Hospital Of Guangxi Medical University
- Class Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Beta-thalassaemia
- Phase 0 Sickle cell anaemia
Most Recent Events
- 21 Aug 2024 Phase-0 for Sickle cell anaemia (In children, In adolescents, In adults) in China (Parenteral) (NCT06565026)
- 18 Jun 2024 Children's Hospital of Fudan University initiates a clinical trial for Beta-thalassemia (In Children, In adolescents) in China (Parenteral) (NCT06479616)
- 13 Jun 2024 Adverse events and efficacy data from a phase I trial in Beta-thalassaemia presented at the 29th Congress of the European Haematology Association (EHA-2024)