CS 101
Alternative Names: CS-101Latest Information Update: 13 Dec 2024
At a glance
- Originator CorrectSequence Therapeutics
- Developer CorrectSequence Therapeutics; The First Affiliated Hospital Of Guangxi Medical University
- Class Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Beta-thalassaemia
- Phase 0 Sickle cell anaemia
Most Recent Events
- 05 Dec 2024 CorrectSequence Therapeutics initiates enrolment in an observational trial for Beta-Thalassemia in China (NCT06717932)
- 12 Nov 2024 CorrectSequence Therapeutics initiates enrolment in a long-term clinical trial for Beta-thalassaemia (In adolescents, In adults, In children) in China (Parenteral), (NCT06685536)
- 21 Aug 2024 Phase-0 for Sickle cell anaemia (In children, In adolescents, In adults) in China (Parenteral) (NCT06565026)