VGB Ex01
Alternative Names: Autologous CRISPR-Cas12b - Shanghai Vitalgen BioPharma; VGB Ex01 - autologous CRISPR-Cas12b; VGB-Ex01Latest Information Update: 08 Dec 2023
At a glance
- Originator Shanghai Vitalgen BioPharma
- Class Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Gene modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Clinical Phase Unknown Thalassaemia
Most Recent Events
- 22 Sep 2023 Preclinical trials in Thalassaemia in China (Parenteral) prior to September 2023 (Shanghai Vitalgen Biopharma pipeline, September 2023)
- 18 Sep 2023 Shanghai Vitalgen BioPharma in collaboration with Institute of Hematology & Blood Diseases Hospital plans a clinical trial for Thalassemia in China (NCT06041620)
- 31 Aug 2023 Clinical trials in Thalassaemia (In children, In adults) in China (Parenteral) (NCT06041620)