Transthyretin amyloidosis gene therapy - Huidagene Therapeutics
Alternative Names: ATTR - Huidagene TherapeuticsLatest Information Update: 26 Oct 2023
At a glance
- Originator HuidaGene Therapeutics
- Class Gene therapies
- Mechanism of Action Gene expression modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Research Transthyretin-related hereditary amyloidosis
Most Recent Events
- 12 Sep 2023 Transthyretin amyloidosis gene therapy - Huidagene Therapeutics is available for licensing as of 12 Sep 2023. https://www.huidagene.com/licensing
- 12 Sep 2023 Early research in Transthyretin-related hereditary amyloidosis in China, prior to September 2023 (Parenteral) (Huidagene Therapeutics pipeline, September 2023)