ENTR 601 50
Alternative Names: ENTR-601-50Latest Information Update: 17 Nov 2025
At a glance
- Originator Entrada Therapeutics
- Class Drug conjugates; Oligonucleotides
- Mechanism of Action Dystrophin expression modulators
-
Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 17 Nov 2025 Entrada Therapeutics plans to initiate phase I/II ELEVATE-50-201 trial for Duchenne muscular dystrophy in the United Kingdom (Parenteral)
- 07 Nov 2025 Entrada Therapeutics filed for regulatory authorization in U.K. to initiate phase I/II ELEVATE-50-201 trial
- 06 Nov 2025 Entrada Therapeutics plans files an IND application with the European Medicines Agency for Duchenne Muscular Dystrophy in the second half of 2026 (Parenteral)