ENTR 601 50
Alternative Names: ENTR-601-50Latest Information Update: 19 Jan 2026
At a glance
- Originator Entrada Therapeutics
- Class Drug conjugates; Oligonucleotides
- Mechanism of Action Dystrophin expression modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 09 Jan 2026 MHRA and Research Ethics Committee approves IND application for ENTR 601 50 in Duchenne muscular dystrophy
- 17 Nov 2025 Entrada Therapeutics plans to initiate phase I/II ELEVATE-50-201 trial for Duchenne muscular dystrophy in the United Kingdom (Parenteral)
- 07 Nov 2025 Entrada Therapeutics filed for regulatory authorization in U.K. to initiate phase I/II ELEVATE-50-201 trial