ENTR 601 51
Alternative Names: ENTR-601-51; Exon 51 - Entrada Therapeutics; Exon 51 skipping oligonucleotide - Entrada TherapeuticsLatest Information Update: 11 Mar 2025
At a glance
- Originator Entrada Therapeutics
- Class Oligonucleotides
- Mechanism of Action Dystrophin expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Duchenne muscular dystrophy
Most Recent Events
- 27 Feb 2025 Preclinical trials in Duchenne muscular dystrophy in USA (Parenteral) (Entrada Therapeutics pipeline, February 2025)
- 27 Feb 2025 Entrada Therapeutics indents to submit regulatory applications for ENTR 601 51 in Duchenne muscular dystrophy in 2026
- 12 Sep 2023 Early research in Duchenne muscular dystrophy in USA(Parenteral) before September 2023 (Entrada Therapeutics pipeline, September 2023)