Research programme: Krabbe disease therapeutics - Apteeus
Alternative Names: Krabbe disease therapeutics - ApteeusLatest Information Update: 13 Oct 2023
At a glance
- Originator APTEEUS
- Class
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Globoid cell leukodystrophy
Most Recent Events
- 25 Sep 2023 Early research in Globoid cell leukodystrophy in France (unspecified route), prior to September 2023 (Apteeus pipeline, September 2023)