CCM 914
Alternative Names: CCM-914; NV-914Latest Information Update: 06 Oct 2023
At a glance
- Originator Italian Cystic Fibrosis Foundation; University of Palermo
- Developer CCM Protein Upregulation
- Class Benzamides; Fluorine compounds; Oxadiazoles; Phenols; Small molecules
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator expression stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Cystic fibrosis
- Research Duchenne muscular dystrophy
Most Recent Events
- 05 Oct 2023 Chemical structure information added
- 25 Sep 2023 CCM Protein Upregulation has patent protection for CCM 914 in US and Europe (CCM Biosciences website, September 2023)
- 25 Sep 2023 Early research in Duchenne muscular dystrophy in USA (PO) prior to September 2023 (CCM Protein Upregulation pipeline, September 2023)