Research programme: non-coding RNAs targeting small molecule therapeutics - NextRNA Therapeutics
Latest Information Update: 09 Oct 2025
At a glance
- Originator NextRNA Therapeutics
- Class Antineoplastics; Small molecules
- Mechanism of Action Long noncoding RNA modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Cancer; Immunological disorders; Neurological disorders
Most Recent Events
- 31 Aug 2025 Discontinued for Cancer in USA (unspecified route)
- 31 Aug 2025 Discontinued for Immunological disorders in USA (unspecified route)
- 31 Aug 2025 Discontinued for Neurological disorders in USA (unspecified route)