Haemophilia A therapeutic - Bayer/CRISPR Therapeutics
Alternative Names: CRISPR/Cas9 haemophilia A therapeuticLatest Information Update: 24 Nov 2023
At a glance
- Originator Casebia Therapeutics
- Developer Bayer; Casebia Therapeutics; CRISPR Therapeutics
- Class Antihaemorrhagics; Gene therapies
- Mechanism of Action Factor VIII expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Haemophilia A
Most Recent Events
- 20 Oct 2023 Early research in Haemophilia A in Switzerland (Parentral) (CRISPR Therapeutics pipeline, October 2023)