VX 828
Alternative Names: VX-828Latest Information Update: 17 Apr 2025
At a glance
- Originator Vertex Pharmaceuticals
- Class Antifibrotics
- Mechanism of Action Undefined mechanism
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Cystic fibrosis
Most Recent Events
- 01 Apr 2025 Phase-I clinical trials in Cystic fibrosis (In volunteers) in USA (PO, Tablet) (NCT06861413)
- 01 Apr 2025 Vertex Pharmaceuticals initiates enrolment in a phase-I clinical trial for Cystic fibrosis (In volunteers) in USA (PO, Suspension) (NCT06861413)
- 25 Mar 2025 Vertex Pharmaceuticals plans a phase I trial for Cystic fibrosis (In volunteers) in March 2025 (PO) (NCT06861413)