LY M003
Alternative Names: LY-M003Latest Information Update: 18 Jun 2026
At a glance
- Originator Lingyi Biotech
- Class Gene therapies
- Mechanism of Action Copper-transporting ATPase replacements; Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Hepatolenticular degeneration
Most Recent Events
- 18 Jun 2026 Lingyi Biotech plans a phase I/II trial for Hepatolenticular degeneration (Treatment experienced) (IV) in June 2026 (NCT07641140)
- 11 Nov 2025 Efficacy and adverse events data from phase I trial for hepatolenticular degeneration presentation at the Liver Meeting 2025: 76th Annual Meeting of the American Association for the Study of Liver Diseases (AASLD-2025)
- 24 Sep 2024 Phase-I for Hepatolenticular degeneration (Treatment experienced, In children, In adolescent, In adults) in China (IV) (NCT06650319)