NG 001
Alternative Names: NG-001Latest Information Update: 06 Mar 2024
At a glance
- Originator Base Therapeutics
- Class Gene therapies; Haematopoietic stem cells therapies
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Beta-thalassaemia; Sickle cell anaemia
Most Recent Events
- 03 Jan 2024 Early research in Beta-thalassaemia in China (Parenteral) prior to January 2024 (Base Therapeutics pipeline, January 2024)
- 03 Jan 2024 Early research in Sickle cell anaemia in China (Parenteral) prior to January 2024 (Base Therapeutics pipeline, January 2024)