CS 201
Alternative Names: CS-201Latest Information Update: 11 Dec 2025
At a glance
- Originator CorrectSequence Therapeutics
- Class Gene therapies
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Unspecified
Most Recent Events
- 11 Dec 2025 Discontinued - Preclinical for Unspecified in China (Parenteral), before December 2025 (CorrectSequence Therapeutics pipeline, December 2025)
- 17 Jan 2024 Preclinical trials in Unspecified in China (Parenteral) before January 2024 (CorrectSequence Therapeutics pipeline, January 2024)