Research programme: gene editing therapeutics - Intellia Therapeutics/ReCode Therapeutics
Latest Information Update: 26 Feb 2024
At a glance
- Originator Intellia Therapeutics; ReCode Therapeutics
- Class Gene therapies
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Cystic fibrosis