APL 3007
Alternative Names: APL-3007Latest Information Update: 15 Oct 2025
At a glance
- Originator Apellis Pharmaceuticals
- Class Eye disorder therapies; Small interfering RNA
- Mechanism of Action Complement C3 expression inhibitors; RNA interference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase II Dry macular degeneration
Most Recent Events
- 23 Jun 2025 Phase-II clinical trials in Dry macular degeneration(Treatment-experienced, Combination therapy) in USA (SC) (NCT07215390)
- 28 Feb 2025 Apellis Pharmaceuticals plans a phase II trial in Dry macular degeneration (Combination thearpy) in 2Q 2025
- 27 Feb 2024 Phase-I clinical trials in Dry macular degeneration (SC) in USA before February 2024