APL 3007
Alternative Names: APL-3007Latest Information Update: 13 Mar 2025
At a glance
- Originator Apellis Pharmaceuticals
- Class Eye disorder therapies; Small interfering RNA
- Mechanism of Action Complement C3 expression inhibitors; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Age-related macular degeneration