SB 007
Alternative Names: SB-007Latest Information Update: 13 Mar 2024
At a glance
- Originator Splice Bio
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action ABCA4 protein modulators; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Stargardt disease
Most Recent Events
- 05 Mar 2024 Preclinical trials in Stargardt disease in Spain (Parenteral), prior to March 2024 (SpliceBio pipeline, March 2024)