NGGT 001
Alternative Names: NGGT-001Latest Information Update: 03 Dec 2024
At a glance
- Originator Xiamen University
- Developer Next Generation Gene Therapeutics; Xiamen University
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Cytochrome P-450 Family 4 replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Bietti crystalline dystrophy
Most Recent Events
- 21 Mar 2024 Phase-I/II clinical trials in Bietti crystalline dystrophy in China (Subretinal) (NCT06706427)
- 08 Feb 2023 Phase-I clinical trials in Bietti crystalline dystrophy in China (Subretinal) (NCT06302608)