Galsulfase biosimilar - GENERIUM Pharmaceuticals
Alternative Names: GEN 071; GNR-071Latest Information Update: 08 Aug 2025
At a glance
- Originator GENERIUM Pharmaceuticals
- Class Arylsulfatases; Recombinant proteins
- Mechanism of Action N acetylgalactosamine 4 sulfatase replacements
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase III Mucopolysaccharidosis VI
Most Recent Events
- 12 Jul 2023 Phase-III clinical trials in Mucopolysaccharidosis VI in Russia (Infusion) (GSZ-MLS-III) (GENERIUM Pharmaceuticals pipeline, August 2025)