SPG 601
Alternative Names: SPG-601Latest Information Update: 21 Jan 2025
At a glance
- Originator Spinogenix
- Class Small molecules
- Mechanism of Action Large conductance calcium activated potassium channel agonists
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase II Fragile X syndrome
Most Recent Events
- 14 Jan 2025 SPG 601 receives Fast Track designation for Fragile X syndrome [PO,Pill,Once daily] (Treatment-experienced) in USA
- 31 Dec 2024 Spinogenix completes phase-II clinical trials in Fragile X syndrome (Treatment-experienced) in USA (PO) (NCT06413537)
- 18 Jun 2024 Phase-II clinical trials in Fragile X syndrome (Treatment-experienced) in USA (PO) (NCT06413537)