Research programme: alpha-1-antitrypsin-deficiency therapeutics - Congruence Therapeutics
Latest Information Update: 10 May 2024
At a glance
- Originator Congruence Therapeutics
- Class Small molecules
- Mechanism of Action Alpha 1-antitrypsin modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Alpha 1-antitrypsin deficiency
Most Recent Events
- 26 Apr 2024 Early research in Alpha 1-antitrypsin deficiency in Canada (unspecified route) (Congruence Therapeutics pipeline; April 2024)