IMSB 301
Alternative Names: IMSB-301Latest Information Update: 16 Feb 2026
At a glance
- Originator ImmuneSensor
- Class Anti-inflammatories; Small molecules
- Mechanism of Action CGAS protein inhibitors
-
Orphan Drug Status
Yes - Aicardi-Goutieres syndrome
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Aicardi-Goutieres syndrome; Autoimmune disorders
- Preclinical Inflammation
Most Recent Events
- 12 Feb 2026 Phase-I clinical trials in Aicardi-Goutieres-syndrome in Australia (PO)
- 12 Jan 2026 Phase-I clinical trials in Autoimmune disorders (Monotherapy, In adolescents, In adult and In the elderly) in Australia (PO) (NCT07364513)
- 20 Nov 2024 IMSB 301 receives Orphan Drug status for Aicardi-Goutieres-syndrome in USA