Antisense oligonucleotide therapeutic - Creyon Bio
Latest Information Update: 13 May 2024
At a glance
- Originator Creyon Bio
- Class Antisense oligonucleotides
- Mechanism of Action Gene silencing; TNPO2 protein expression inhibitors
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Clinical Phase Unknown Neurological disorders