ABO 204
Alternative Names: ABO-204Latest Information Update: 03 Jun 2024
At a glance
- Originator Arbor Biotechnologies
- Class Gene therapies
- Mechanism of Action Gene expression modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Amyotrophic lateral sclerosis
Most Recent Events
- 23 May 2024 Early research in Amyotrophic lateral sclerosis in USA (Parenteral)