RGT 61159
Alternative Names: RGT-61159Latest Information Update: 19 Sep 2025
At a glance
- Originator Rgenta Therapeutics
- Class Antineoplastics; Small molecules
- Mechanism of Action Proto-oncogene protein c-myb expression inhibitors; RNA splicing modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Adenoid cystic carcinoma; Colorectal cancer
- Preclinical Acute myeloid leukaemia
Most Recent Events
- 19 Sep 2025 RGT 61159 receives Orphan Drug status for Adenoid cystic carcinoma in USA
- 12 Jun 2025 Pharmacodynamics data from a preclinical trial in Acute myeloid leukaemia released by Rgenta Therapeutics
- 25 Apr 2025 Pharmacodynamics data from preclinical trial in Acute myeloid leukemia presented at the 116th Annual Meeting of the American Association for Cancer Research (AACR-2025)