OPGx MERTK
Alternative Names: AAV2-VMD2-hMERTK; OPGx-MERTKLatest Information Update: 29 Jun 2026
At a glance
- Originator Opus Genetics
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action C-Mer tyrosine kinase replacements; Gene transference
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Orphan Drug Status
No
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Retinitis pigmentosa
Most Recent Events
- 17 Jun 2026 Pharmacodynamics data from a preclinical study in Retinitis pigmentos released by Opus Genetics
- 17 Jun 2026 Opus Genetics plans a clinical trial for Retinitis pigmentosa in United Arab Emirates (Subretinal) in the first quarter of 2027
- 23 Jun 2025 Opus genetics plans to initiate Investigational New Drug (IND) enabling studies in Retinitis pigmentosa