Research programme: Anti-CD19 CAR therapies - Orna Therapeutics
Latest Information Update: 12 Jun 2025
At a glance
- Originator Orna Therapeutics
- Class Cell therapies; Gene therapies; RNA
- Mechanism of Action Cell replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Autoimmune disorders