BMS 986470
Alternative Names: BMS-986470Latest Information Update: 20 Feb 2025
At a glance
- Originator Bristol-Myers Squibb
- Class Antianaemics; Small molecules
- Mechanism of Action Apoptosis stimulants; CRBN protein modulators; Fetal haemoglobin expression modulators; Ubiquitin protein ligase modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I/II Sickle cell anaemia
Most Recent Events
- 07 Dec 2024 Pharmacodynamics data from a preclinical trial in Sickle cell anaemia presented at the 66th American Society of Hematology Annual Meeting and Exposition (ASH-Hem-2024)
- 17 Jul 2024 Phase-I/II clinical trials in Sickle cell anaemia in USA (PO) (NCT06481306)
- 17 Jul 2024 Preclinical trials in Sickle cell anaemia in USA (PO) prior to July 2024