KER 0193
Alternative Names: KER-0193Latest Information Update: 27 May 2025
At a glance
- Originator Kaerus Bioscience
- Class Behavioural disorder therapies; Small molecules
- Mechanism of Action Large conductance calcium activated potassium channel modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Fragile X syndrome
Most Recent Events
- 14 May 2025 KER 0193 receives Orphan Drug status for Fragile X syndrome in USA
- 14 May 2025 KER 0193 receives Rare Pediatric Drug designation for Fragile X syndrome in USA
- 11 Mar 2025 Safety, pharmacodynamics and pharmacokinetics data from a phase I trial in Fragile X syndrome (In volunteers) released by Kaerus Bioscience